AQUINO, Fábio Oliveira; SILVA, Ricardo Eccard; NOVAES, Maria Rita. Public Policies for Rare Diseases in Brazil: Regulatory Path, Challenges in Research and Access to Orphan Drugs. Journal of Hospital Pharmacy and Health Services, [S. l.], v. 16, n. 3, p. e1300, 2025. DOI: 10.30968/jhphs.2025.163.1300. Disponível em: https://jhphs.org/sbrafh/article/view/1300. Acesso em: 1 dec. 2025.